Improving the lives of those with phenylketonuria (PKU) through clinical research.
Find a Clinical Site Near You
Participants make it possible for researchers to find new treatments, speed diagnosis and improve the lives of those affected by rare diseases.
Learn More
Join the RDCRN for FDA-NIH Rare Disease Day, February 27-28, 2025
Don’t miss the in-person and virtual celebration of
Rare Research Report: October 2024
Each month, we share summaries of recent Rare Diseases Clinical Research Network (RDCRN) grant-funded publications.
Rare Research Report: September 2024
Each month, we share summaries of recent Rare Diseases Clinical Research Network (RDCRN) grant-funded publications.