Improving the lives of those with phenylketonuria (PKU) through clinical research.

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Participants make it possible for researchers to find new treatments, speed diagnosis and improve the lives of those affected by rare diseases.

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Each month, we share summaries of recent Rare Diseases Clinical Research Network (RDCRN) grant-funded publications.

Each month, we share summaries of recent Rare Diseases Clinical Research Network (RDCRN) grant-funded publications.