Improving the lives of those with phenylketonuria (PKU) through clinical research.

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Participants make it possible for researchers to find new treatments, speed diagnosis and improve the lives of those affected by rare diseases.
Learn MoreJoin RDCRN at Rare Disease Day at NIH on February 28
Don’t miss the in-person and virtual celebration of

Training Program for Clinical Research in Rare Disease Launches New Session
The National Institutes of Health-funded R25 Rare Disease Clinical Research Training Program is launching a new training program for clinical resea
